Onasemnogene abeparvovec

Onasemnogene abeparvovec is a gene therapy medicine designed to treat spinal muscular atrophy (SMA), a rare genetic disorder that causes progressive muscle weakness and paralysis. The drug works by delivering a functi…

1 Articles
2 min read
Wikipedia
Key Facts
🧠
Field
Medicine
📅
First proposed
2019
Impact
Moderate
📚
Articles
1
Covered Disciplines
Medicine
1

Onasemnogene abeparvovec

Onasemnogene abeparvovec is a gene therapy medicine designed to treat spinal muscular atrophy (SMA), a rare genetic disorder that causes progressive muscle weakness and paralysis. The drug works by delivering a functi…

1 Articles
2 Concepts
2 min read
Wikipedia
Key Facts
🧠
Field
Medicine
📅
First proposed
2019
Impact
Moderate
📚
Articles
1